A special lifesaving drug Only A $41 is sold abroad (about RMB 205)Domestic sales of 700000?
Recently, a media release of "medicine" information has attracted wide attention. Hunan a baby boy who has just turned 1 year old is lying in the hospital for more than 9 months because of a rare disease," spinal muscular atrophy (SMA)", which is in urgent need of special medicine to save a life, and the special drug Gnostic sodium injection needs 700000 yuan. This puts ordinary boy families on the verge of despair.
What kind of medicine is this? Why is the gap so big at home and abroad?
In order to find out the domestic pricing of Gnostic sodium, a mother of Guangdong, Ms. Ouyang, submitted an application to the State Drug Administration for disclosure of information such as the pricing of Gnostic sodium. Another lawyer has also applied to the State Drug Administration for disclosure of relevant pricing information, in response to the lawyer, the Chinese Drug Administration said that the pricing of the drug is not within the scope of acceptance of the National Drug Administration, proposed to apply to the National Development and Reform Commission for information disclosure, but also said that drug pricing is a market behavior
What kind of medicine is noxynasheng sodium injection?
Gnostic sodium injection (Nusinersen) is the first approved SMA treatment drug in the world. As of June 30, 2020, Gnostic sodium injection has been approved in 50 countries and regions and has been reimbursed in more than 40 countries and regions.
According to experts, Gnostic sodium injection is an antisense nucleotide therapy for type 5 q spinal muscular atrophy in infants, children and adults, and is also the first imported drug approved for the treatment of spinal muscular atrophy in China. Doctors use intrathecal injection (through the lumbar puncture to inject drugs into the body) to give patients medication.
Children need to use drugs as soon as possible after diagnosis:6 times in the first year,4 injections in the first 2 months, and 1 injection every 4 months. Some children in injection after medication, exercise ability has a certain degree of recovery. A 2-year-old 11-month-old boy in Hunan province began injecting the drug in May and has been injected four times. After treatment, the motor ability of Nono was recovered well. "It's certainly useful in treatment, but it does n' t completely reverse the condition ."
Why is the drug so expensive?
Gnostic sodium injection was approved for import in 2019 and is not currently included in health. In China, the price per unit of the drug is 699700 yuan.
According to the newly revised drug management law in 2019, the drug price is no longer priced by the government but mainly regulated by the market, which plays a role through centralized bidding and procurement of medical insurance. Song Hualin, vice president of Nankai University Law School and expert in drug law, said that the number of patients with rare diseases is small and there is clinical uncertainty, so the cost of drug development is high and the price of drugs is expensive. Individual pharmaceutical enterprises often get pricing advantage because of technology leading, which does not necessarily violate China's anti-monopoly law or drug regulatory laws and regulations. He believes that the deep reason why rare diseases often attract attention is that the types of rare diseases that can be covered by medical insurance are limited, and commercial medical insurance in China still needs to be improved at the present stage, and the medical needs of patients with rare diseases are difficult to fully meet.
According to the staff of the Office of Letters and visits of the State Medical Insurance Bureau, Gnostic sodium injection has been included in the medical insurance negotiation schedule since its domestic listing in 2019, and the state hopes to negotiate with relevant pharmaceutical enterprises to reduce the price of drugs. And then meet the needs of SMA patients.
Is the price of Chinese patients expected to decline?
Last year, the country began negotiations with pharmaceutical companies, by the expert group to study pricing, the specific pricing is not clear. But the inclusion of health care has not been discussed, because drug prices do not come, there is always no way to enter the health care catalog.
Why can't pharmaceutical companies be included in health care without falling prices? The staff of the Office of Letters and visits of the State Medical Insurance Bureau further explained to reporters that the medical insurance catalog developed by the State Medical Insurance Bureau is applicable to all parts of the country, so it is necessary to ensure that the drugs entered into the medical insurance catalog can be used everywhere. "Once such rare drugs are included in the health care catalog, for less developed regions, when the fund is used to pay for high-priced rare diseases, other underlying diseases may not be guaranteed, and subsequent local economic pressures may be created, so the most fundamental solution is for the state to negotiate with pharmaceutical companies and negotiate prices ."
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